FIELD: medicine.
SUBSTANCE: group of inventions refers to medicine and concerns using a polynucleotide which contains a sequence coding a C-terminal heavy subunit domain of tetanus toxin (HcTeTx), for treating amyotrophic lateral sclerosis (ALS), as well as using a polynucleotide which contains a C-terminal of a heavy subunit of tetanus toxin (HcTeTx), for treating the above disease.
EFFECT: group of inventions provides relieving the ALS symptoms ensured by introducing an isolated non-toxic fragment of tetanus toxin (HcTeTx or a fragment thereof) or the polynucleotide coding the above fragment.
17 cl, 4 ex, 11 dwg, 2 tbl
Title |
Year |
Author |
Number |
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|
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2012 |
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|
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2006 |
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|
RU2410087C2 |
GENE THERAPY OF NEURODEGENERATIVE DISORDERS |
2010 |
- Passini, Marco, A.
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|
RU2743398C2 |
GENE THERAPY OF NEURODEGENERATIVE DISORDERS |
2021 |
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|
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GENE THERAPY FOR NEURODEGENERATIVE DISORDERS |
2010 |
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|
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VECTORS AND SEQUENCES FOR TREATING DISEASES |
2011 |
- Bosh Tubert Fatima
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|
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THERAPEUTIC AGENT FOR AMYOTROPHIC LATERAL SCLEROSIS |
2013 |
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|
RU2655811C2 |
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2014 |
|
RU2639582C2 |
IMMUNOGEN FOR PREVENTING OR TREATING FAMILIAL FRONTOTEMPORAL DEMENTIA (FTD) AND/OR AMYOTROPHIC LATERAL SCLEROSIS (ALS) |
2020 |
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|
RU2833931C2 |