FIELD: medicine.
SUBSTANCE: claimed invention relates to medicine, namely to therapy, and deals with treatment of lysosomal storage disease - Niemann-Pick A or B disease. For this purpose enzyme acid sphingometlinaise is slowly, for three hours, introduced intraventricularly.
EFFECT: method and mode of introduction provide effective treatment of said disease due to reduction of pathological level of acid sphingomyelinase substrate both in tissues of brain and in visceral organs.
9 cl, 13 dwg, 5 tbl, 6 ex
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