FIELD: biotechnologies.
SUBSTANCE: offered hydroxylamine derivative which, in particular, can be bimoclomol, arimoclomol or their structural analogues, amplifies Hsp70 gene expression and thus increases intracellular concentration of Hsp70. The offered medicament, which is hydroxylamine derivative, is capable to increase intracellular concentration of Hsp70, reverse in efficient way the pathology of lysosomal storage disorders. The offered hydroxylamine derivative and the medicament can be used for treatment of lysosomal storage disorders.
EFFECT: increase of intracellular concentration of Hsp70.
18 cl, 16 dwg, 2 tbl, 3 ex
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