FIELD: medicine; pharmaceutics.
SUBSTANCE: invention relates to medicine and pharmaceutics, namely to use of a composition containing a therapeutically effective amount of alpha-1-antitrypsin protein (AAT) and at least one pharmaceutical carrier for treating and/or preventing Charcot-Marie-Tooth disease.
EFFECT: treatment or prevention of Charcot-Marie-Tooth disease.
4 cl, 19 dwg, 22 tbl, 16 ex
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Authors
Dates
2025-05-26—Published
2022-05-03—Filed