VECTORS CONDITIONALLY EXPRESSING THERAPEUTIC PROTEINS, HOST CELLS COMPRISING THE VECTORS, AND USES THEREOF Russian patent published in 2017 - IPC C12N15/63 A61K48/00 A61P35/00 

Abstract RU 2612788 C2

FIELD: medicine.

SUBSTANCE: present invention relates to gene therapy for treating eye diseases, more specifically to use vectors for conditional expression of one or more therapeutic protein under the control of gene expression modulation system in the presence of activating ligand in the preparing of a drug, and can be used in medicine.

EFFECT: present invention allows to engineer a conditional expression vectors, which can be used for treating macular degeneration or glaucoma in an individual.

10 cl, 40 dwg, 8 tbl, 12 ex

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Authors

Dates

2017-03-13Published

2011-03-23Filed