VIRAL VECTORS ENCODING RECOMBINANT FIX VARIANTS WITH INCREASED EXPRESSION FOR GENE THERAPY OF HEMOPHILIA B Russian patent published in 2022 - IPC C12N15/11 C12N15/86 C07K14/745 A61K48/00 A61P7/04 

Abstract RU 2773956 C2

FIELD: biotechnology.

SUBSTANCE: invention relates to the field of biotechnology, specifically to polynucleotide encoding factor IX protein; it can be used in medicine. Polynucleotide contains a nucleic acid sequence that is at least 99% identical to a nucleic acid sequence SEQ ID NO: 17.

EFFECT: obtained polynucleotide can be used in the composition of a vector for effective gene therapy of hemophilia B in mammals.

26 cl, 25 dwg, 7 tbl, 6 ex

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RU 2 773 956 C2

Authors

Horling, Franziska

Lengler, Johannes

Falkner, Falko-Gunther

Rottensteiner, Hanspeter

Scheiflinger, Friedrich

Dates

2022-06-14Published

2018-05-22Filed