FIELD: biotechnology.
SUBSTANCE: invention relates to the field of biotechnology, specifically to polynucleotide encoding factor IX protein; it can be used in medicine. Polynucleotide contains a nucleic acid sequence that is at least 99% identical to a nucleic acid sequence SEQ ID NO: 17.
EFFECT: obtained polynucleotide can be used in the composition of a vector for effective gene therapy of hemophilia B in mammals.
26 cl, 25 dwg, 7 tbl, 6 ex
Title | Year | Author | Number |
---|---|---|---|
IX PADUA FACTOR ANTIBODIES | 2017 |
|
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Authors
Dates
2022-06-14—Published
2018-05-22—Filed