FIELD: biotechnology.
SUBSTANCE: adeno-associated virus (hereinafter – AAV) containing capsid protein, a composition for the treatment of a muscle-related disease or disorder, a method for the delivery of a transgene to a muscle cell, a method for the treatment of a subject suffering from a muscle-related disorder or disease, an expression vector, a cell for the expression of AAV capsid protein, the use of AAV in the manufacture of a drug for the treatment of a muscle-related disorder or diseases; cDNA containing a nucleotide sequence encoding capsid protein, a method for targeting a transgene to a muscle cell, and a method for the production of an adeno-associated virus (AAV) are presented.
EFFECT: invention allows for the use of an adeno-associated virus (AAV) in gene therapy methods.
72 cl, 10 tbl, 3 ex
| Title |
Year |
Author |
Number |
| NEW LIVER TARGETING ADENO-ASSOCIATED VIRAL VECTORS |
2019 |
- Colosi, Peter Cameron
- Ramirez, Silvia
|
RU2793735C2 |
| RECOMBINANT VIRAL PARTICLES WITH MODIFIED TROPISM AND WAYS OF THEIR USE FOR TARGETED INTRODUCTION OF GENETIC MATERIAL INTO HUMAN CELLS |
2018 |
- Sabin, Lea
- Shonerr, Kristofer
- Ekonomides, Aris N.
- Kiratsus, Kristos
- Merfi, Endryu Dzh.
|
RU2811426C2 |
| VERSIONS BASED ON ADENO-ASSOCIATED VIRUS, COMPOSITIONS AND METHODS FOR PULMONARY DELIVERY |
2021 |
- Kotterman, Melissa
- Francis, Peter
- Calton, Melissa
- Gonzales, Johnny
- Croze, Roxanne
- Schmitt, Christopher
|
RU2829874C1 |
| COMPOSITIONS AND METHODS FOR INCREASING OR ENHANCING TRANSDUCTION OF GENE THERAPY VECTORS AND FOR REMOVING OR REDUCING IMMUNOGLOBULINS |
2021 |
|
RU2841237C1 |
| RECOMBINANT VIRAL VECTORS WITH MODIFIED TROPISM AND WAYS OF THEIR USE FOR TARGETED INTRODUCTION OF GENETIC MATERIAL INTO HUMAN CELLS |
2018 |
- Kiratsus, Kristos
- Merfi, Endryu Dzh.
- Vang, Cheng
- Sabin, Lea
|
RU2809246C2 |
| COMPOSITION FOR RELIEVING OR TREATING PAIN |
2017 |
- Kim, Sujeong
- Choi, Heonsik
- Kwon, Yejin
- Kim, Minjung
- Kim, Minju
- Kim, Daewook
- Park, Jangjoon
- Cho, Jongho
- Lee, Soondong
- Kim, Joonsung
- Sim, Yeomoon
|
RU2725830C1 |
| GENE THERAPY OF HYPOPHOSPHATEMIC DISEASES ASSOCIATED WITH FIBROBLAST GROWTH FACTOR 23 |
2020 |
- Rontsitti, Dzhuzeppe
- Zhoz, Luiza
- Sharl, Severin
- Mingotstsi, Frederiko
|
RU2815545C2 |
| GENOTHERAPY CONSTRUCTIONS FOR TREATMENT OF WILSON'S DISEASE |
2020 |
- Livingston, Christine
- Wadsworth, Samuel
|
RU2807158C2 |
| VERSION OF AAV, COMPOSITIONS AND METHODS IN WHICH IT IS USED, AS WELL AS METHODS OF USING IT FOR TRANSFERRING GENES INTO CELLS, ORGANS AND TISSUES |
2014 |
- High, Katherine A.
- Yazicioglu, Mustafa N.
- Anguela, Xavier
|
RU2837753C2 |
| TREATMENT OF COMPLEMENT-MEDIATED DISORDERS |
2017 |
- Lachmann, Peter
- Alexander, Ian
|
RU2768982C2 |
