FIELD: biotechnology.
SUBSTANCE: there are presented: a vector containing a nucleic acid construct, a cell, and a pharmaceutical composition for treating FGF-23 related hypophosphatemic diseases, in particular XLH, by means of gene therapy.
EFFECT: invention can be effectively used for gene therapy of FGF-23 related hypophosphatemic diseases, in particular, gene therapy aimed at muscle, hepatic or hematopoietic tissue, more specifically, at liver tissue.
17 cl, 1 tbl, 6 dwg, 1 ex
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