FIELD: biotechnology.
SUBSTANCE: group of inventions is described, including an adeno-associated virus (AAV) for retinal cell transduction, a pharmaceutical composition for gene transfer into retinal cells, the use of AAV for the treatment of damage to photoreceptor cells, the in vitro use of AAV for retinal cell nucleus transduction, and a kit for gene transfer into retinal cells.
EFFECT: invention expands the arsenal of agents for retinal cell transduction.
14 cl, 16 dwg, 2 tbl, 6 ex
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