FIELD: medicine.
SUBSTANCE: expressing cassette is proposed containing an isolated nucleic acid molecule containing or consisting of a nucleic acid sequence SEQ ID NO: 1 functionally connected to at least a nucleic acid sequence encoding a gene, where the specified isolated nucleic acid molecule is effective for directing the gene expression in a rod photoreceptor cell. A vector containing the specified expressing cassette is proposed. A method for expressing a gene in a rod photoreceptor cell and use of the expressing cassette for expressing a gene in a rod photoreceptor cell are proposed.
EFFECT: proposed group of inventions provides for the control of expressing operatively bound gene in a rod photoreceptor cell through a functionally connected isolated nucleic acid molecule.
8 cl, 1 dwg, 1 ex
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Authors
Dates
2021-10-26—Published
2016-12-01—Filed